Tag: voxelotor

The FDA has approved two new drugs to treat sickle cell disease. They don’t do much, and they are prohibitively expensive.  Sickle cell disease is a serious condition, an abnormality of hemoglobin that is inherited in an autosomal recessive pattern, where both parents have to pass on the defective gene.… read more "New Drugs for Sickle Cell Disease: Small Benefit, Large Price"